HMS scientists are pursuing three gene therapies with the hope that at least one will treat progressive blindness caused by Usher syndrome type 1F.

Version that includes an audio-description:    • Finding Treatment for a Rare Genetic ...  

Find out more at https://hms.harvard.edu/news/pursuing...

00:00 What is Usher syndrome Type 1F?
00:53 Inspiration for the project
02:28 Gene therapy and the challenge of finding a treatment
03:37 Three approaches
05:05 Toward a cure